Drugs / HG005
last change Aug 2025 re-read 3 minutes ago

HG005

Gene therapy (AAV / viral vector) targets ABCA4 via restoration

Developed for
Stargardt disease
Investigated by
HuidaGene Therapeutics Co., Ltd.

Trials 1

20262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 0 NCT07063251 Aug 2025 → Feb 2027 expected Stargardt disease HuidaGene Therapeutics Co., Ltd. Recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as HG005 ClinicalTrials.gov intervention name — accepted as the source's own label NCT07063251 ↗
Action Restore “The goal of HG005 is to restore normal waste removal, protect retinal cells from further damage, and slow or stop vision loss.” NCT07063251 ↗
Modality Gene therapy (AAV / viral vector) “HG005 used two AAV vectors that work together in retinal cells to produce the full-length, functional ABCA4 protein.” NCT07063251 ↗
Target ABCA4 “HG005 is an investigational gene therapy designed to deliver a healthy copy of the ABCA4 gene to the retina.” NCT07063251 ↗