Drugs / BAMOCAFTOR
last change Sep 2020 re-read 2 minutes ago

BAMOCAFTOR

Small molecule targets CFTR via restoration

Developed for
cystic fibrosis
Investigated by
Vertex Pharmaceuticals Incorporated

Trials 6 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT03029455 Nov 2016 → Aug 2017 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 21 trial
Phase 2 NCT03224351 Aug 2017 → Feb 2018 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 34 trials
Phase 3 NCT03633526 Aug 2018 → Jan 2019 cystic fibrosis Vertex Pharmaceuticals Incorporated Terminated No outcome recorded
Phase 3 NCT03447262 Jul 2018 → Sep 2020 cystic fibrosis Vertex Pharmaceuticals Incorporated Terminated No outcome recorded
Phase 3 NCT03460990 May → Sep 2018 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 3 NCT03447249 Mar 2018 → Feb 2019 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded

Press releases naming this drug 5 releases

DateIssuerRelease
2018-11-27 Vertex Pharmaceuticals Incorporated Two Phase 3 Studies of the Triple Combination of VX-659, Tezacaftor and Ivacaftor Met Primary Endpoint of Improvement in Lung Function (ppFEV1) in People with Cystic Fibrosis vrtx.com
2018-09-06 Vertex Pharmaceuticals Incorporated Vertex Completes Enrollment of Two Phase 3 Studies of VX-659 in Triple Combination with Tezacaftor and Ivacaftor for the Treatment of Cystic Fibrosis vrtx.com
2018-03-01 Vertex Pharmaceuticals Incorporated Vertex Initiates Phase 3 Study of VX-659, Tezacaftor and Ivacaftor as a Triple Combination Regimen for People with Cystic Fibrosis Who Have Two Copies of the F508del Mutation vrtx.com
2018-02-21 Vertex Pharmaceuticals Incorporated Vertex Initiates First Phase 3 Study of VX-659, Tezacaftor and Ivacaftor as a Triple Combination Regimen for People with Cystic Fibrosis vrtx.com
2018-02-01 Vertex Pharmaceuticals Incorporated Vertex Selects Two Next-Generation Correctors, VX-659 and VX-445, to Advance into Phase 3 Development as Part of Two Different Triple Combination Regimens for People with Cystic Fibrosis vrtx.com

Evidence & citations 9 cited values

Every value below carries the sentence it was read from. 8 sources stand behind the page.

FieldValueCited text
Known as BAMOCAFTOR ChEMBL registry synonym — accepted as the source's own label CHEMBL4297849
Known as BAMOCAFTOR POTASSIUM ChEMBL registry synonym — accepted as the source's own label CHEMBL4297849
Known as VX-659 ClinicalTrials.gov intervention name — accepted as the source's own label NCT03447249
5

NCT03633526

NCT03447262

NCT03224351

NCT03460990

NCT03029455

Known as VX-659 POTASSIUM ChEMBL registry synonym — accepted as the source's own label CHEMBL4297849
Known as VX-659 potassium salt ChEMBL registry synonym — accepted as the source's own label CHEMBL4297849
Action Restore “was developed to restore the function of Phe508del CFTR protein” PMID 30334693 Oct 2018
Modality Small molecule CHEMBL4297849
Route Oral “A range of oral VX-659-tezacaftor-ivacaftor doses in triple combination were then evaluated” PMID 30334693 Oct 2018
Target CFTR “was developed to restore the function of Phe508del CFTR protein” PMID 30334693 Oct 2018