Drugs / BAF312

Regulatory milestones approvals, filings & regulatory actions · 3 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansion US (FDA) MAYZENT 2022-03-01 fda.gov
Approved EU (EMA) Mayzent 2020-01-13 europa.eu
Approved US (FDA) MAYZENT 2019-03-26 fda.gov

Trials 17 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 13 trials
Phase 1 NCT01904214 Jul 2013 → Nov 2014 impaired renal function disease Novartis Pharmaceuticals Completed No outcome recorded
Phase 1 NCT01565902 Oct 2012 → Mar 2014 Novartis Pharmaceuticals Completed No outcome recorded
Phase 1 NCT00422175 Oct 2006 → Nov 2007 Novartis Completed No outcome recorded
Phase 27 trials
Phase 2 NCT06639282 Aug 2025 → Oct 2029 expected Alzheimer disease St. Joseph's Hospital and Medical Center, Phoenix Recruiting No outcome recorded
Phase 2 NCT03338998 Dec 2017 → May 2020 intracerebral hemorrhage Novartis Pharmaceuticals Completed No outcome recorded
Phase 2 NCT02029274 Aug 2013 → Feb 2016 dermatomyositis Novartis Pharmaceuticals Terminated No outcome recorded
Phase 2 NCT01801917 Apr 2013 → Aug 2016 polymyositis Novartis Pharmaceuticals Terminated No outcome recorded
Phase 2 NCT01185821 Aug 2010 → Oct 2016 relapsing-remitting multiple sclerosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 2 NCT01148810 Jun 2010 → Jun 2012 dermatomyositis Novartis Pharmaceuticals Terminated No outcome recorded
Phase 2 NCT00879658 Mar 2009 → May 2011 relapsing-remitting multiple sclerosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 33 trials
Phase 3 NCT04926818 Oct 2021 → Mar 2026 overdue multiple sclerosis Novartis Pharmaceuticals Active not recruiting No outcome recorded
Phase 3 NCT03623243 Feb 2019 → Jul 2022 multiple sclerosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 3 NCT01665144 Dec 2012 → Apr 2016 secondary progressive multiple sclerosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 42 trials
Phase 4 NCT04792567 Apr → Sep 2021 secondary progressive multiple sclerosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 4 NCT03535298 Jan 2019 → Jul 2027 expected relapsing-remitting multiple sclerosis The Cleveland Clinic Active not recruiting No outcome recorded
Phase not applicable1 trial
NCT00162474 Sep 2003 → Dec 2030 expected Hadassah Medical Organization Recruiting No outcome recorded
Phase not stated1 trial
NCT04540861 multiple sclerosis Novartis Pharmaceuticals No longer available No outcome recorded

Press releases naming this drug 10 releases

DateIssuerRelease
2020-09-11 Novartis Pharmaceuticals Novartis data show early treatment with Mayzent® (siponimod) delays disability progression and show benefits in cognitive performance in patients with secondary progressive multiple sclerosis (SPMS) novartis.com
2020-04-21 Novartis Pharmaceuticals Novartis announces new Mayzent® (siponimod) data show sustained effect in delaying disability for up to five years in patients with secondary progressive multiple sclerosis (SPMS) novartis.com
2020-01-20 Novartis Pharmaceuticals Novartis announces EU approval of Mayzent® (siponimod) for adult patients with secondary progressive multiple sclerosis (SPMS) with active disease novartis.com
2019-11-15 Novartis Pharmaceuticals Novartis receives positive CHMP opinion for Mayzent® (siponimod) for the treatment of adult patients with active secondary progressive multiple sclerosis (SPMS) novartis.com
2019-03-27 Novartis Pharmaceuticals Novartis receives FDA approval for Mayzent® (siponimod), the first oral drug to treat secondary progressive MS with active disease novartis.com
2018-10-08 Novartis Pharmaceuticals Novartis announces FDA and EMA filing acceptance of siponimod, the first and only drug shown to meaningfully delay disability progression in typical SPMS patients novartis.com
2018-04-20 Novartis Pharmaceuticals New Novartis analyses at AAN show siponimod's efficacy on disability and cognition in secondary progressive MS patients novartis.com
2018-03-23 Novartis Pharmaceuticals Phase III data in The Lancet show Novartis siponimod significantly improves outcomes in patients with secondary progressive MS novartis.com
2016-09-17 Novartis Pharmaceuticals Novartis BAF312 reduces the risk of disability progression in pivotal phase III study in secondary progressive MS patients novartis.com
2016-08-25 Novartis Pharmaceuticals Novartis announces positive phase III results showing efficacy of BAF312 in patients with secondary progressive MS novartis.com

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 19 sources stand behind the page.

FieldValueCited text
Known as BAF312 “Siponimod (formerly known as BAF312 and completed trial NCT #01665144) has been FDA approved since 2019 (IND #076122) for the treatment of multiple sclerosis.” NCT06639282
11

“Siponimod (BAF312)” NCT01665144

NCT00879658

NCT01801917

NCT01904214

NCT01148810

NCT01565902

NCT01185821

NCT04792567

NCT03338998

NCT00422175

NCT02029274

Known as Mayzent (siponimod) Mayzent (siponimod)NCT03535298
Known as siponimod Siponimod is a sphingosine 1-phosphate receptor modulator approved for active secondary progressive multiple sclerosis (aSPMS) in most countries” PMID 35639197 May 2022
7

Siponimod for patients with relapsing-remitting multiple sclerosis (BOLD): an adaptive, dose-ranging, randomised, phase 2 study.” PMID 23764350 Jun 2013

“Mayzent (siponimod)” NCT03535298

NCT04926818

NCT04540861

NCT06639282

NCT03623243

NCT00162474

Route Oral oral BAF312” NCT00422175