Drugs / Rondaptivon Pegol
last change Jul 2026 re-read 2 minutes ago

Rondaptivon Pegol

Aptamer targets VWF via inhibition

Developed for
hemophilia A · von Willebrand disease (hereditary or acquired) · von Willebrand disease type 2B
Investigated by
Medical University of Vienna · Band Therapeutics

Trials 3 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT04103034 Oct 2019 → Sep 2020 intracranial arteriosclerosis, large artery stroke Band Therapeutics Completed No outcome recorded
Phase 22 trials
Phase 2 NCT07273721 Aug 2025 → Jul 2026 overdue von Willebrand disease type 2B Medical University of Vienna Recruiting No outcome recorded
Phase 2 NCT04677803 Dec 2020 → Sep 2021 hemophilia A, von Willebrand disease (hereditary or acquired) Medical University of Vienna Completed No outcome recorded

Evidence & citations 9 cited values

Every value below carries the sentence it was read from. 6 sources stand behind the page.

FieldValueCited text
Known as Rondaptivon Pegol “Efficacy and Safety of BT200 (Rondaptivon Pegol) in Patients With Type 2B Von Willebrand Disease” NCT07273721
Known as BT-200 FREE ACID ChEMBL registry synonym — accepted as the source's own label CHEMBL5314642
Known as BT200 ClinicalTrials.gov intervention name — accepted as the source's own label NCT04677803
2

NCT04103034

NCT07273721

Known as Rondaptivon pegol sodium ChEMBL registry synonym — accepted as the source's own label CHEMBL5314642
Known as rondoraptivon pegol Rondoraptivon pegol (BT200) is a pegylated aptamer binding to the A1 domain of VWF with a novel mechanism of action: it enhances VWF/factor VIII (FVIII) levels by decreasing...” PMID 35772170 Sep 2022
1

“Efficacy and Safety of BT200 (Rondoraptivon Pegol) in Patients With Type 2B Von Willebrand Disease” NCT07273721

Action Inhibit “This trial identified a novel mechanism of action for BT200: BT200 dose-dependently increases VWF/FVIII by prolonging half-life at doses well below those which inhibit...” PMID 34818873 Sep 2022
Modality Aptamer “A new VWF A1-domain binding aptamer, BT200, demonstrated good subcutaneous bioavailability and a long half-life in non-human primates.” PMID 34818873 Sep 2022
Route Subcutaneous “Subjects will receive a single subcutaneous dose of BT200 0.18mg” NCT04103034
Target VWF “A new VWF A1-domain binding aptamer, BT200, demonstrated good subcutaneous bioavailability and a long half-life in non-human primates.” PMID 34818873 Sep 2022