Phase 0 1 trial
Phase 0
NCT04424966
Jul 2020 → Jan 2023
glioblastoma
Nader Sanai
Terminated
No outcome recorded
Phase 1 7 trials
Phase 1
NCT05510427
Aug 2023
cholangiocarcinoma
M.D. Anderson Cancer Center
Withdrawn
No outcome recorded
Phase 1
NCT04972253
Dec 2021 → Dec 2022
bladder transitional cell carcinoma
Guru P. Sonpavde
Withdrawn
No outcome recorded
Phase 1
NCT04504331
Oct 2020 → Oct 2021
Her2-receptor negative breast cancer , estrogen-receptor positive breast cancer , progesterone-receptor positive breast cancer
Jennifer Lee Caswell-Jin
Terminated
No outcome recorded
Phase 1
NCT02312804
Jan 2015
cervical carcinoma
The University of Texas Health Science Center at San Antonio
Withdrawn
No outcome recorded
Phase 1
NCT01928459
Oct 2013 → Aug 2016
cancer , metastatic neoplasm
Novartis Pharmaceuticals
Completed
No outcome recorded
Phase 1
NCT01697605
Oct 2012 → Feb 2019
—
Novartis Pharmaceuticals
Completed
No outcome recorded
Phase 1
NCT01004224
Dec 2009 → Oct 2018
squamous cell lung carcinoma , urinary bladder cancer
Novartis Pharmaceuticals
Completed
No outcome recorded
Phase 1/2 4 trials
Phase 1/2
NCT05222165
Oct 2021 → Dec 2022
central nervous system neoplasm , grade II glioma
Helsinn Healthcare SA
Withdrawn
No outcome recorded
Phase 1/2
NCT04228042
Jul 2020 → Apr 2024
renal pelvis/ureter urothelial carcinoma
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Phase 1/2
NCT02257541
Oct 2014 → Mar 2019
gastrointestinal stromal tumor
Memorial Sloan Kettering Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT02575508
? → May 2020
colon adenocarcinoma , pancreatic ductal adenocarcinoma , rectum adenocarcinoma
Roswell Park Cancer Institute
Withdrawn
No outcome recorded
Phase 2 14 trials
Phase 2
NCT07393373
Apr 2026 → May 2036 expected
hypochondroplasia
QED Therapeutics, a BridgeBio company
Enrolling by invitation
No outcome recorded
Phase 2
NCT07169279
Nov 2025 → Mar 2030 expected
achondroplasia
QED Therapeutics, a BridgeBio company
Recruiting
No outcome recorded
Phase 2
NCT05514912
Mar 2024 → Jun 2027
intrahepatic cholangiocarcinoma
Emory University
Withdrawn
No outcome recorded
Phase 2
NCT06206278
Oct 2023 → May 2024
gastric cancer , gastroesophageal junction adenocarcinoma
LianBio LLC
Terminated
No outcome recorded
Phase 2
NCT05145010
Dec 2021 → Dec 2031 expected
achondroplasia
QED Therapeutics, a BridgeBio company
Enrolling by invitation
No outcome recorded
Phase 2
NCT05019794
May 2020 → Dec 2022
gastric cancer , gastroesophageal junction adenocarcinoma
LianBio LLC
Unknown
No outcome recorded
Phase 2
NCT04265651
Mar 2020 → Oct 2024
achondroplasia
QED Therapeutics, a BridgeBio company
Completed
No outcome recorded
Phase 2
NCT04233567
Jan 2020 → Dec 2023
cholangiocarcinoma , metastatic malignant neoplasm
Sameek Roychowdhury
Completed
No outcome recorded
Phase 2
NCT03510455
Feb 2019 → Feb 2020
Oncogenic osteomalacia
National Institute of Dental and Craniofacial Research (NIDCR)
Terminated
No outcome recorded
Phase 2
NCT02706691
Jun 2018 → Feb 2019
human papilloma virus infection , nasopharyngeal carcinoma , oropharynx squamous cell carcinoma
University of Chicago
Terminated
No outcome recorded
Phase 2
NCT02160041
Jul 2014 → Apr 2018
cancer , hematopoietic and lymphoid cell neoplasm
Novartis Pharmaceuticals
Terminated
No outcome recorded
Phase 2
NCT02150967
Jul 2014 → Mar 2021
cholangiocarcinoma
QED Therapeutics, a BridgeBio company
Terminated
No outcome recorded
Phase 2
NCT02159066
Jul 2014 → Jan 2023
melanoma
Pfizer
Completed
No outcome recorded
Phase 2
NCT01975701
Dec 2013 → Oct 2018
malignant glioma
Novartis Pharmaceuticals
Completed
No outcome recorded
Show 4 more trials
Phase 2/3 1 trial
Phase 2/3
NCT06873035
Apr 2025 → Jan 2027 expected
hypochondroplasia
QED Therapeutics, a BridgeBio company
Enrolling by invitation
No outcome recorded
Phase 3 3 trials
Phase 3
NCT06164951
Nov 2023 → Dec 2025
achondroplasia
QED Therapeutics, a BridgeBio company
Completed
No outcome recorded
Phase 3
NCT04197986
Mar 2020 → Feb 2023
infiltrating bladder urothelial carcinoma , infiltrating renal pelvis/ureter urothelial carcinoma
QED Therapeutics, a BridgeBio company
Terminated
No outcome recorded
Phase 3
NCT03773302
Dec 2019 → Mar 2023
cholangiocarcinoma
QED Therapeutics, a BridgeBio company
Terminated
No outcome recorded
Phase not applicable 1 trial
—
NCT02657486
Jan 2016 → Feb 2026
non-invasive bladder urothelial carcinoma
Memorial Sloan Kettering Cancer Center
Completed
No outcome recorded