Drugs / rAAV2/4.hRPE65
last change Aug 2014 re-read 3 minutes ago

rAAV2/4.hRPE65

Gene therapy (AAV / viral vector)

Developed for
Leber congenital amaurosis
Investigated by
Nantes University Hospital

Trials 1

2012201320142015201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT01496040 Sep 2011 → Aug 2014 Leber congenital amaurosis Nantes University Hospital Completed No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as rAAV2/4.hRPE65 ClinicalTrials.gov intervention name — accepted as the source's own label NCT01496040 ↗
Modality Gene therapy (AAV / viral vector) “Clinical Gene Therapy Protocol” NCT01496040 ↗
Route Other “single subretinal injection” NCT01496040 ↗