Drugs / RGX-121-3102
last change Nov 2025 re-read 3 minutes ago

RGX-121-3102

targets IDS

Developed for
mucopolysaccharidosis type 2
Investigated by
REGENXBIO Inc.

Trials 1

202620272028
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 3 NCT07236606 Nov 2025 → Apr 2028 expected mucopolysaccharidosis type 2 REGENXBIO Inc. Active not recruiting No outcome recorded

Evidence & citations 2 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as RGX-121-3102 ClinicalTrials.gov intervention name — accepted as the source's own label NCT07236606 ↗
Target IDS “RGX-121 is a gene therapy which is intended to deliver a functional copy of the iduronate-2-sulfatase gene (IDS) to the central nervous system.” NCT07236606 ↗