drugset
Drugs / β-globin restored autologous HSC
last change Jul 2022 re-read 3 minutes ago

β-globin restored autologous HSC

CRISPR / gene editing

Developed for
beta-thalassemia major
Investigated by
Bioray Laboratories · The 923rd Hospital of Joint Logistics Support Force of People's Liberation Army

Trials 1

today NCT04205435 · Ph 1/2
20222023202420252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT04205435 Nov 2021 → Jun 2022 beta-thalassemia major Bioray Laboratories Terminated No outcome recorded Stop: Business

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as β-globin restored autologous HSC ClinicalTrials.gov intervention name — accepted as the source's own label NCT04205435 ↗
Action Restore “gene edited autologous hematopoietic stem cells with β-globin restoration” NCT04205435 ↗
Modality CRISPR / gene editing “manufactured using CRISPR/Cas9 gene editing system” NCT04205435 ↗