Drugs / AAV-MECP2
last change Jan 2025 re-read 3 minutes ago

AAV-MECP2

Gene therapy (AAV / viral vector) targets MECP2

Developed for
Rett syndrome
Investigated by
Guangzhou Women and Children's Medical Center

Trials 1

20252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 0 NCT06856759 Jan 2025 → Oct 2026 expected Rett syndrome Guangzhou Women and Children's Medical Center Active not recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as AAV-MECP2 ClinicalTrials.gov intervention name — accepted as the source's own label NCT06856759 ↗
Modality Gene therapy (AAV / viral vector) “AAV-MECP2 gene therapy product for RTT” NCT06856759 ↗
Route Intrathecal “Administration route: intrathecal injection” NCT06856759 ↗
Target MECP2 “recombinant AAV gene therapy vector containing neuron specific promoter (CAG) driven MECP2” NCT06856759 ↗