Drugs / tividenofusp alfa
last change Jan 2026 re-read 2 minutes ago

tividenofusp alfa

also known as DNL310 · Etv:ids

Protein / enzyme biologic

Developed for
mucopolysaccharidosis type 2
Investigated by
Denali Therapeutics Inc.

Trials 3 · a red edge is where a trial was stopped

20212022202320242025202620272028202920302031
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/21 trial
Phase 1/2 NCT04251026 Jul 2020 → Feb 2031 expected mucopolysaccharidosis type 2 Denali Therapeutics Inc. Active not recruiting No outcome recorded
Phase 2/32 trials
Phase 2/3 NCT06075537 Sep 2023 → Jun 2027 expected mucopolysaccharidosis type 2 Denali Therapeutics Inc. Enrolling by invitation No outcome recorded
Phase 2/3 NCT05371613 Jul 2022 → Dec 2027 expected mucopolysaccharidosis type 2 Denali Therapeutics Inc. Recruiting No outcome recorded

Evidence & citations 5 cited values

Every value below carries the sentence it was read from. 5 sources stand behind the page.

FieldValueCited text
Known as tividenofusp alfa ClinicalTrials.gov intervention name — accepted as the source's own label NCT06075537
2

NCT04251026

NCT05371613

Known as DNL310 “This is a multicenter, multiregional, open-label study to assess the safety, pharmacokinetics (PK), and pharmacodynamics (PD) of tividenofusp alfa (DNL310), an investigational...” NCT04251026
1

“tividenofusp alfa (DNL310), an investigational central nervous system (CNS)-penetrant enzyme-replacement therapy (ERT)” NCT05371613

Known as Etv:ids ChEMBL registry synonym — accepted as the source's own label CHEMBL4594537
Modality Protein / enzyme biologic “Tividenofusp alfa, comprising iduronate-2-sulfatase fused to an engineered transferrin receptor-binding Fc domain” PMID 41467650 Jan 2026
Route Intravenous Intravenous repeating dose” NCT04251026