Drugs / BIIB111
last change Jun 2026 re-read 3 minutes ago

BIIB111

Gene therapy (AAV / viral vector)

Developed for
choroideremia
Investigated by
Biogen · NightstaRx Ltd, a Biogen Company

Trials 2

2018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 3 NCT03584165 Jun 2018 → Jun 2026 choroideremia, retinitis pigmentosa NightstaRx Ltd, a Biogen Company Completed No outcome recorded
Phase 3 NCT03496012 Dec 2017 → Dec 2020 choroideremia Biogen Completed Missed primary

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 2 sources stand behind the page.

FieldValueCited text
Known as BIIB111 ClinicalTrials.gov intervention name — accepted as the source's own label NCT03496012 ↗
1

NCT03584165 ↗

Modality Gene therapy (AAV / viral vector) “Retinal Gene Therapy for Choroideremia Using an Adeno-Associated Viral Vector (AAV2) Encoding Rab Escort Protein 1 (REP1)” NCT03496012 ↗
Route Other “through sub-retinal injection” NCT03496012 ↗