Drugs / GEN6050X
last change Dec 2025 re-read 3 minutes ago

GEN6050X

targets DMD

Developed for
Duchenne muscular dystrophy
Investigated by
Peking Union Medical College Hospital

Trials 1

20252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 0 NCT06392724 Jul 2024 → Dec 2025 overdue Duchenne muscular dystrophy Peking Union Medical College Hospital Active not recruiting No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as GEN6050X ClinicalTrials.gov intervention name — accepted as the source's own label NCT06392724 ↗
Route Intravenous “GEN6050X is an intravenously administered human DMD exon 50 skipping base editing drug.” NCT06392724 ↗
Target DMD “GEN6050X is an intravenously administered human DMD exon 50 skipping base editing drug.” NCT06392724 ↗