Drugs / baliforsen
last change Mar 2023 re-read 3 minutes ago

baliforsen

Developed for
myotonic dystrophy type 1
Investigated by
Ionis Pharmaceuticals, Inc.

Trials 1

2015201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT02312011 Dec 2014 → Jul 2016 myotonic dystrophy type 1 Ionis Pharmaceuticals, Inc. Completed No outcome recorded

Evidence & citations 5 cited values

Every value below carries the sentence it was read from. 2 sources stand behind the page.

FieldValueCited text
Known as baliforsen “We aimed to investigate the safety of baliforsen (ISIS 598769), an ASO targeting DMPK mRNA.” PMID 36804094 ↗ Mar 2023
Known as IONIS-598769 FREE ACID ChEMBL registry synonym — accepted as the source's own label CHEMBL3990009 ↗
Known as IONIS598769 ChEMBL registry synonym — accepted as the source's own label CHEMBL3990009 ↗
Known as ISIS 598769 FREE ACID ChEMBL registry synonym — accepted as the source's own label CHEMBL3990009 ↗
Route Subcutaneous “subcutaneous injections of baliforsen 100 mg” PMID 36804094 ↗ Mar 2023