Drugs / NTF001
last change Apr 2026 re-read 3 minutes ago

NTF001

Gene therapy (AAV / viral vector) targets NDNF

Developed for
amyotrophic lateral sclerosis
Investigated by
Ruijin Hospital

Trials 1

20272028
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1 NCT07618585 Apr 2026 → Mar 2028 expected amyotrophic lateral sclerosis Ruijin Hospital Active not recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as NTF001 ClinicalTrials.gov intervention name — accepted as the source's own label NCT07618585 ↗
Modality Gene therapy (AAV / viral vector) “AAV-mediated gene therapy product” NCT07618585 ↗
Route Intrathecal “administered once by intrathecal injection” NCT07618585 ↗
Target NDNF “designed to express human neuron-derived neurotrophic factor (NDNF)” NCT07618585 ↗