Drugs / AAV2-hCHM
last change Oct 2022 re-read 3 minutes ago

AAV2-hCHM

Gene therapy (AAV / viral vector) targets CHM

Developed for
choroideremia
Investigated by
Spark Therapeutics, Inc.

Trials 1

2015201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT02341807 Jan 2015 → Oct 2022 choroideremia Spark Therapeutics, Inc. Completed No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 2 sources stand behind the page.

FieldValueCited text
Known as AAV2-hCHM ClinicalTrials.gov intervention name — accepted as the source's own label NCT02341807 ↗
Modality Gene therapy (AAV / viral vector) “recombinant adeno-associated virus serotype 2 (AAV2) vector” PMID 35714735 ↗ Jun 2022
Route Other “subretinal administration of AAV2-hCHM” NCT02341807 ↗
Target CHM “a human CHM-encoding cDNA (AAV2-hCHM)” PMID 35714735 ↗ Jun 2022