Drugs / VGM-R02b
last change Apr 2024 re-read 3 minutes ago

VGM-R02b

Gene therapy (AAV / viral vector)

Developed for
glutaryl-CoA dehydrogenase deficiency
Investigated by
Shanghai Vitalgen BioPharma Co., Ltd.

Trials 1

202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1 NCT06217861 Apr 2024 → Aug 2027 expected glutaryl-CoA dehydrogenase deficiency Shanghai Vitalgen BioPharma Co., Ltd. Recruiting No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as VGM-R02b ClinicalTrials.gov intervention name — accepted as the source's own label NCT06217861 ↗
Modality Gene therapy (AAV / viral vector) “VGM-R02b is an adeno-associated viral vector 9 delivering human Glutaryl-CoA Dehydrogenase (GCDH) gene.” NCT06217861 ↗
Route Other “intra-cerebroventricular injection could also be used for drug administration” NCT06217861 ↗