Drugs / Unesbulin
last change Jul 2024 re-read 2 minutes ago

Unesbulin

also known as PTC596 · Bmi1 inhibitor ptc596

Small molecule targets BMI1 via inhibition

Developed for
leiomyosarcoma · cancer · diffuse intrinsic pontine glioma · high grade astrocytic tumor · ovarian cancer
Investigated by
PTC Therapeutics · Nationwide Children's Hospital · University of Oklahoma

Trials 5 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 14 trials
Phase 1 NCT03761095 Mar 2019 → Feb 2024 leiomyosarcoma PTC Therapeutics Completed No outcome recorded
Phase 1 NCT03605550 Aug 2018 → Mar 2024 overdue diffuse intrinsic pontine glioma, high grade astrocytic tumor Nationwide Children's Hospital Active not recruiting No outcome recorded
Phase 1 NCT03206645 Aug 2017 → Aug 2021 ovarian cancer University of Oklahoma Completed No outcome recorded
Phase 1 NCT02404480 Jan 2016 → Feb 2017 cancer PTC Therapeutics Completed No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT05269355 May 2022 → Jun 2024 leiomyosarcoma PTC Therapeutics Terminated No outcome recorded

Evidence & citations 7 cited values

Every value below carries the sentence it was read from. 6 sources stand behind the page.

FieldValueCited text
Known as Unesbulin “The goal of this study is to evaluate the safety of the study drug PTC596 (Unesbulin) taken in combination with radiotherapy (RT) when given to pediatric patients newly...” NCT03605550
3

NCT05269355

NCT03206645

NCT03761095

Known as Bmi1 inhibitor ptc596 ChEMBL registry synonym — accepted as the source's own label CHEMBL4594353
Known as PTC596 ClinicalTrials.gov intervention name — accepted as the source's own label NCT02404480
1

NCT03605550

Action Inhibit “To test the ability of PTC596 to inhibit BMI-1 activity in tumor and PBMCs” NCT03605550
Modality Small molecule CHEMBL4594353
Route Oral “administered orally” NCT02404480
Target BMI1 “To test the ability of PTC596 to inhibit BMI-1 activity in tumor and PBMCs” NCT03605550