Drugs / Autologous CD34+ cells genetically modified
last change Sep 2021 re-read 3 minutes ago

Autologous CD34+ cells genetically modified

Cell therapy targets HBB

Developed for
beta-thalassemia major
Investigated by
Guangdong Yike Gene Science and Technology CO.,Ltd · Nanfang Hospital, Southern Medical University

Trials 1

2018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT03276455 Sep 2017 → Sep 2020 beta-thalassemia major Nanfang Hospital, Southern Medical University Unknown No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as Autologous CD34+ cells genetically modified ClinicalTrials.gov intervention name — accepted as the source's own label NCT03276455 ↗
Modality Cell therapy “autologous hematopoietic stem cell transduced with lentiviral vector” NCT03276455 ↗
Route Other “The product will be injected intraosseously” NCT03276455 ↗
Target HBB “encoding the therapeutic beta-globin gene” NCT03276455 ↗