Drugs / AMD3100

Regulatory milestones approvals, filings & regulatory actions · 2 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved EU (EMA) Mozobil 2009-07-30 europa.eu
Approved US (FDA) MOZOBIL 2008-12-15 fda.gov

Trials 17 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 13 trials
Phase 1 NCT01655875 Jun 2012 → Apr 2014 childhood acute lymphoblastic leukemia, childhood acute myeloid leukemia Emory University Terminated No outcome recorded
Phase 1 NCT01026987 Apr 2010 → Apr 2014 disease related to hematopoietic stem cell transplant Washington University School of Medicine Completed No outcome recorded
Phase 1 NCT00322127 Jun 2006 → Jan 2015 National Heart, Lung, and Blood Institute (NHLBI) Completed No outcome recorded
Phase 1/25 trials
Phase 1/2 NCT00733824 Nov 2008 → Sep 2012 Hodgkins lymphoma, non-Hodgkin lymphoma Washington University School of Medicine Completed No outcome recorded
Phase 1/2 NCT00512252 Jul 2007 → Jun 2010 acute myeloid leukemia Washington University School of Medicine Completed No outcome recorded
Phase 1/2 NCT00479115 May 2007 → Dec 2010 Fanconi anemia Children's Hospital Medical Center, Cincinnati Completed No outcome recorded
Phase 1/2 NCT00241358 May 2004 → Dec 2009 B-cell chronic lymphocytic leukemia, Hodgkins lymphoma, acute myeloid leukemia, chronic myeloid leukemia +2 Washington University School of Medicine Completed No outcome recorded
Phase 1/2 NCT00396968 acute myeloid leukemia, myelodysplastic syndrome Genzyme, a Sanofi Company Withdrawn No outcome recorded
Phase 25 trials
Phase 2 NCT04058145 Sep → Oct 2019 head and neck squamous cell carcinoma Massachusetts General Hospital Withdrawn No outcome recorded
Phase 2 NCT03055247 Nov 2015 → Jul 2023 overdue granulomatous disease, chronic, X-linked IRCCS San Raffaele Recruiting No outcome recorded
Phase 2 NCT00914849 Aug 2009 → Jan 2011 hematopoietic and lymphoid cell neoplasm Washington University School of Medicine Completed No outcome recorded
Phase 2 NCT00082329 Jun 2004 → Oct 2012 National Heart, Lung, and Blood Institute (NHLBI) Completed No outcome recorded
Phase 2 NCT00075335 Jan 2004 → Aug 2012 National Heart, Lung, and Blood Institute (NHLBI) Completed No outcome recorded
Phase 41 trial
Phase 4 NCT02056210 Feb → Oct 2014 diabetes mellitus University of Padova Completed No outcome recorded
Phase not applicable2 trials
NCT04045821 Jan 2020 → Jan 2021 female infertility of uterine origin Reproductive Medicine Associates of New Jersey Terminated No outcome recorded
NCT01206075 Oct 2010 → Dec 2012 beta-thalassemia major University of Washington Completed No outcome recorded
Phase not stated1 trial
NCT00291811 Oct 2003 → ? disease related to hematopoietic stem cell transplant Genzyme, a Sanofi Company Approved for marketing No outcome recorded
Also used as a comparator or background therapy in 4 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 12 trials
Phase 1 NCT03612466 Background Aug 2022 → Jan 2023 bone neoplasm, osteosarcoma Albert Einstein College of Medicine Withdrawn No outcome recorded
Phase 1 NCT01353937 Comparator Apr 2014 → Mar 2016 ulcer of lower limbs NYU Langone Health Withdrawn No outcome recorded
Phase 1/21 trial
Phase 1/2 NCT00967785 Comparator Jan 2010 → Dec 2026 expected myeloid hemopathy, neutropenia, skin disorder caused by infection National Institute of Allergy and Infectious Diseases (NIAID) Recruiting No outcome recorded
Phase 21 trial
Phase 2 NCT02703779 Background Mar 2016 → Oct 2019 plasma cell myeloma Siddhartha Ganguly Completed No outcome recorded

Evidence & citations 8 cited values

Every value below carries the sentence it was read from. 22 sources stand behind the page.

FieldValueCited text
Known as AMD 3100 “The CXCR4 antagonist plerixafor (AMD3100, Mozobil) durably reverses panleukopenia and in most WHIM patients induces wart regression;” PMID 40330596 Apr 2025
16

“AMD3100 is a new drug that also mobilizes stem cells in large numbers within a few hours.” NCT00082329

AMD 3100 (Mozobil Plerixafor) to Mobilize Stem Cells for Donation” NCT00075335

NCT00322127

NCT00512252

NCT01026987

NCT00396968

NCT00914849

NCT01655875

NCT04058145

NCT00479115

NCT00733824

NCT04045821

NCT00241358

NCT01353937

NCT00291811

NCT00075335

Known as AMD3100 (Plerixafor) AMD3100 (Plerixafor)NCT01353937
Known as Mozobil “This is a pilot (phase 1) study of AMD3100(also called Plerixafor, Mozobil).” NCT01655875
9

“AMD 3100 (Mozobil Plerixafor) to Mobilize Stem Cells for Donation” NCT00075335

“subcutaneous AMD3100 (Plerixafor/Mozobil®)” NCT01353937

“AMD 3100 (Mozobil plerixafor)” NCT00082329

NCT02703779

NCT00967785

NCT02056210

NCT03055247

NCT03612466

NCT01206075

Known as plerixafor “Mozobil (Plerixafor): 0,24 mg/kg daily. When CD34+ are ≥ 10 /μL Plerixafor will be administered subcutaneously from the next day (or from day 24 if CD34+ are \< 10 /μL) to the...” NCT03055247
5

“The objective of this study is to perform a prospective randomized, controlled trial to evaluate the response of the endometrial lining after subcutaneous administration of...” NCT04045821

“This is a pilot (phase 1) study of AMD3100(also called Plerixafor, Mozobil).” NCT01655875

“AMD 3100 (Mozobil Plerixafor) to Mobilize Stem Cells for Donation” NCT00075335

“Mozobil (TM) (plerixafor injection, Genzyme/Sanofi)” NCT00967785

“AMD 3100 (Mozobil plerixafor)” NCT00082329

Action Inhibit inhibits the binding of stromal cell derived factor-1 (SDF-1) to its cognate receptor CXC- chemokine receptor 4 (CXCR4)” NCT00075335
Modality Small molecule “AMD3100, is a bicyclam compound” NCT00075335
Route Subcutaneous “single subcutaneous injection of AMD3100” NCT00075335
Target CXCR4 “AMD3100 reversibly inhibits CXC- chemokine receptor 4 (CXCR4) binding” NCT00082329