Drugs / rAAV2tYF-PR1.7-hCNGB3
last change Jul 2026 re-read 3 minutes ago

rAAV2tYF-PR1.7-hCNGB3

Gene therapy (AAV / viral vector) targets CNGB3

Developed for
achromatopsia
Investigated by
Beacon Therapeutics · National Eye Institute (NEI)

Trials 1

201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT02599922 Apr 2016 → Jul 2022 overdue achromatopsia Beacon Therapeutics Active not recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as rAAV2tYF-PR1.7-hCNGB3 ClinicalTrials.gov intervention name — accepted as the source's own label NCT02599922 ↗
Modality Gene therapy (AAV / viral vector) “recombinant adeno-associated virus vector” NCT02599922 ↗
Route Other “administered to one eye by subretinal injection” NCT02599922 ↗
Target CNGB3 “expresses the CNGB3 gene” NCT02599922 ↗