Drugs / Rilonacept
last change Mar 2025 re-read 2 minutes ago

Rilonacept

Protein / enzyme biologic targets IL1B via inhibition

Developed for
gout · chronic kidney disease · Muckle-Wells syndrome · pericarditis · adult-onset Still disease · alcoholic hepatitis · anemia · atherosclerosis
+15 more · autoimmune inner ear disease · autosomal recessive familial Mediterranean fever · cardiac sarcoidosis · cold urticaria · coronary artery disorder · familial cold autoinflammatory syndrome · familial Mediterranean fever · juvenile idiopathic arthritis · Schnitzler syndrome · systemic-onset juvenile idiopathic arthritis · type 1 diabetes mellitus · bursitis · cardiovascular disorder · diffuse cutaneous systemic sclerosis · diffuse scleroderma
Investigated by
Regeneron Pharmaceuticals · National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) · Kiniksa Pharmaceuticals (UK), Ltd. · Charite University, Berlin, Germany · Johns Hopkins University · Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center
+13 more · Mayo Clinic · Montefiore Medical Center · National Heart, Lung, and Blood Institute (NHLBI) · National Institute on Alcohol Abuse and Alcoholism (NIAAA) · National Institutes of Health Clinical Center (CC) · Southern California Institute for Research and Education · Stanley Cohen · Syneos Health · The Cleveland Clinic · University of Colorado, Denver · University of Southern California · University of Texas Southwestern Medical Center · VA Long Beach Healthcare System

Regulatory milestones approvals, filings & regulatory actions · 5 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansions (2) US (FDA) ARCALYST 2020-12-18 – 2021-03-18 fda.gov
Withdrawn EU (EMA) Rilonacept Regeneron (previously Arcalyst) 2012-10-24 europa.eu
Approved EU (EMA) Rilonacept Regeneron (previously Arcalyst) 2009-10-23 europa.eu
Approved US (FDA) ARCALYST 2008-02-27 fda.gov

Trials 20 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 01 trial
Phase 0 NCT02828033 Feb 2017 → Mar 2018 autoimmune inner ear disease Stanley Cohen Unknown No outcome recorded
Phase 12 trials
Phase 1 NCT00962026 Feb 2011 → Mar 2013 type 1 diabetes mellitus University of Texas Southwestern Medical Center Completed No outcome recorded
Phase 1 NCT01803321 Nov 2005 → Jun 2008 systemic-onset juvenile idiopathic arthritis Regeneron Pharmaceuticals Completed No outcome recorded
Phase 211 trials
Phase 2 NCT06660732 Mar 2025 → Nov 2026 expected cardiac sarcoidosis Mayo Clinic Recruiting No outcome recorded
Phase 2 NCT03980522 Jan 2018 → May 2019 pericarditis Kiniksa Pharmaceuticals (UK), Ltd. Completed No outcome recorded
Phase 2 NCT01903798 Dec 2014 → Apr 2016 alcoholic hepatitis Southern California Institute for Research and Education Completed No outcome recorded
Phase 2 NCT01801449 Feb 2013 → Apr 2016 National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) Completed No outcome recorded
Phase 2 NCT01045772 Jan 2009 → Sep 2010 Muckle-Wells syndrome, Schnitzler syndrome Charite University, Berlin, Germany Completed No outcome recorded
Phase 2 NCT00534495 Nov 2008 → Jun 2013 juvenile idiopathic arthritis Montefiore Medical Center Completed No outcome recorded
Phase 2 NCT00582907 Aug 2008 → Sep 2011 autosomal recessive familial Mediterranean fever The Cleveland Clinic Completed No outcome recorded
Phase 2 NCT00610363 Nov 2007 → Oct 2008 gout Regeneron Pharmaceuticals Completed No outcome recorded
Phase 2 NCT00417417 Dec 2006 → Apr 2008 atherosclerosis, coronary artery disorder National Heart, Lung, and Blood Institute (NHLBI) Completed No outcome recorded
Phase 2 NCT00094900 Oct 2004 → Sep 2010 adult-onset Still disease, familial Mediterranean fever National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) Completed No outcome recorded
Phase 35 trials
Phase 3 NCT03737110 Jan 2019 → May 2020 pericarditis Kiniksa Pharmaceuticals (UK), Ltd. Completed No outcome recorded
Phase 3 NCT01459796 Nov 2011 → Jun 2013 gout Regeneron Pharmaceuticals Terminated No outcome recorded
Phase 3 NCT00958438 Jul 2009 → Dec 2010 gout Regeneron Pharmaceuticals Completed No outcome recorded
Phase 3 NCT00856206 Mar 2009 → Jan 2011 gout Regeneron Pharmaceuticals Completed No outcome recorded
Phase 3 NCT00288704 Dec 2005 → Jun 2008 Muckle-Wells syndrome, cold urticaria, familial cold autoinflammatory syndrome Regeneron Pharmaceuticals Completed No outcome recorded
Phase 41 trial
Phase 4 NCT01663103 Aug 2012 → Dec 2014 chronic kidney disease University of Colorado, Denver Completed No outcome recorded
Also used as a comparator or background therapy in 6 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/21 trial
Phase 1/2 NCT01538719 Comparator Dec 2011 → Jan 2017 diffuse cutaneous systemic sclerosis, diffuse scleroderma Boston University Completed No outcome recorded
Phase 22 trials
Phase 2 NCT02171416 Comparator Jan 2015 → Feb 2018 cold urticaria Charite University, Berlin, Germany Completed No outcome recorded
Phase 2 NCT00897715 Comparator Jan 2013 → Feb 2015 cardiovascular disorder, chronic kidney disease VA Office of Research and Development Completed No outcome recorded
Phase 32 trials
Phase 3 NCT00855920 Comparator Mar 2009 → Feb 2010 gout Regeneron Pharmaceuticals Completed No outcome recorded
Phase 3 NCT00829829 Comparator Feb 2009 → May 2010 gout Regeneron Pharmaceuticals Completed No outcome recorded
Phase not applicable1 trial
NCT01830699 Comparator Mar 2013 → Mar 2014 bursitis Keesler Air Force Base Medical Center Completed No outcome recorded

Evidence & citations 10 cited values

Every value below carries the sentence it was read from. 31 sources stand behind the page.

FieldValueCited text
Known as Rilonacept rilonacept (IL-1 Trap)” PMID 18668591 Aug 2008
25

RilonaceptNCT00288704

NCT01663103

NCT00417417

NCT00582907

NCT01045772

NCT01459796

NCT01803321

NCT00534495

NCT02828033

NCT00829829

NCT06660732

NCT00610363

NCT00958438

NCT00897715

NCT00856206

NCT00855920

NCT00609544

NCT01903798

NCT00288704

NCT01538719

NCT00962026

NCT01830699

NCT02171416

NCT01801449

NCT03737110

Known as Arcalyst “This group will continue Prednisolone (40mg/day). Additionally, they will receive rilonacept (Arcalyst®) once a week for 21 days.” NCT01903798
1

“A Pilot Open-Label Study of Rilonacept (Arcalyst) in the Deficiency of the Interleukin-1 Receptor Antagonist (DIRA)” NCT01801449

Known as IL-1 Trap “OBJECTIVE: To evaluate the efficacy and safety of IL-1 inhibitor rilonacept (IL-1 Trap) for gout flare (GF) prevention during initiation of uric acid-lowering therapy (ULT)...” PMID 23485476 Mar 2013
3

“the interleukin (IL-1) blocker, rilonacept (IL-1 Trap), demonstrated efficacy for gout flare prevention during initiation of urate-lowering therapy.” PMID 23375025 Feb 2013

“rilonacept (IL-1 Trap)” NCT01803321

“rilonacept (IL-1 Trap)” PMID 18668591 Aug 2008

Known as interleukin-1 Trap “Efficacy and safety of rilonacept (interleukin-1 Trap) in patients with cryopyrin-associated periodic syndromes: results from two sequential placebo-controlled studies.” PMID 18668535 Aug 2008
1

“interleukin-1 inhibitor rilonacept (interleukin-1 Trap)” PMID 18668591 Aug 2008

Known as KPL-914 ClinicalTrials.gov intervention name — accepted as the source's own label NCT03980522
Known as Rilonacept regeneron (previously arcalyst) ChEMBL registry synonym — accepted as the source's own label CHEMBL1201830
Action Inhibit “The interleukin-1 inhibitor rilonacept” PMID 23031624 Sep 2012
1

“Interleukin-1 beta inhibitor” CHEMBL1201830

Modality Protein / enzyme biologic “investigational biological agent, rilonacept” NCT00417417
Route Subcutaneous “weekly subcutaneous rilonacept 160 mg” PMID 23031624 Sep 2012
Target IL1B “Interleukin-1 beta inhibitor” CHEMBL1201830