Drugs / AAV8.hLCA5
last change Jun 2023 re-read 3 minutes ago

AAV8.hLCA5

Gene therapy (AAV / viral vector)

Developed for
Leber congenital amaurosis 5
Investigated by
Opus Genetics, Inc · University of Pennsylvania

Trials 1

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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT05616793 Jun 2023 → Jun 2028 expected Leber congenital amaurosis 5 Opus Genetics, Inc Recruiting No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as AAV8.hLCA5 ClinicalTrials.gov intervention name — accepted as the source's own label NCT05616793 ↗
Modality Gene therapy (AAV / viral vector) “Adeno-associated virus vector expressing human LCA5 gene” NCT05616793 ↗
Route Other “subretinal injection” NCT05616793 ↗