Drugs / Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene
Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene
targets WAS via restoration
Trials 1
| Phase | Registry id | Dates | Indication | Sponsor | Status | Outcome |
|---|---|---|---|---|---|---|
| Phase 1/2 | NCT01347346 | May 2011 → Jan 2016 | Wiskott-Aldrich syndrome | Genethon | Completed | Met primary |
Evidence & citations 3 cited values
Every value below carries the sentence it was read from. 2 sources stand behind the page.
| Field | Value | Cited text |
|---|---|---|
| Known as | Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene | ClinicalTrials.gov intervention name — accepted as the source's own label NCT01347346 ↗ |
| Action | Restore | “gene therapy through the provision of gene-corrected, autologous hematopoietic stem/progenitor cells” PMID 35075289 ↗ Jan 2022 |
| Target | WAS | “transplantation of patient's autologous CD34+ cells transduced with lentiviral vector containing human WAS gene” NCT01347346 ↗ |