Drugs / nL-TUBB4-001

Trials 2

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT07222371 Sep 2025 → Sep 2027 expected TUBB4A-related neurologic disorder University of California, San Diego Active not recruiting No outcome recorded
Phase 1/2 NCT06369974 Sep 2024 → Jun 2026 overdue disease of genetic or genomic mechanism Massachusetts General Hospital Enrolling by invitation No outcome recorded

Evidence & citations 2 cited values

Every value below carries the sentence it was read from. 2 sources stand behind the page.

FieldValueCited text
Known as nL-TUBB4-001 “Drug: nL-TUBB4-001; Personalized antisense oligonucleotide” NCT06369974 ↗
1

NCT07222371 ↗

Modality Antisense oligonucleotide “personalized antisense oligonucleotide (ASO) drug” NCT06369974 ↗