Drugs / GC310
last change Oct 2025 re-read 3 minutes ago

GC310

Gene therapy (AAV / viral vector) targets ATP7B via restoration

Developed for
Wilson disease
Investigated by
GeneCradle Inc

Trials 1

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT07173933 Oct 2025 → Apr 2027 expected Wilson disease GeneCradle Inc Not yet recruiting No outcome recorded

Evidence & citations 5 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as GC310 ClinicalTrials.gov intervention name — accepted as the source's own label NCT07173933 ↗
Action Restore “delivering a functional copy of the truncated human ATP7B gene” NCT07173933 ↗
Modality Gene therapy (AAV / viral vector) “GC310 is an adeno-associated virus 5 (AAV5) vector delivering a functional copy of the truncated human ATP7B gene” NCT07173933 ↗
Route Intravenous “Participants will be administrated GC310 intravenously” NCT07173933 ↗
Target ATP7B “GC310 is an adeno-associated virus 5 (AAV5) vector delivering a functional copy of the truncated human ATP7B gene” NCT07173933 ↗