Drugs / gene transduced PBL and/or gene transduced HSC
Trials 1
| Phase | Registry id | Dates | Indication | Sponsor | Status | Outcome |
|---|---|---|---|---|---|---|
| Phase 1/2 | NCT00599781 | Mar 1992 → Jul 2006 | severe combined immunodeficiency | IRCCS San Raffaele | Completed | No outcome recorded |
Evidence & citations 4 cited values
Every value below carries the sentence it was read from. 2 sources stand behind the page.
| Field | Value | Cited text |
|---|---|---|
| Known as | gene transduced PBL and/or gene transduced HSC | ClinicalTrials.gov intervention name — accepted as the source's own label NCT00599781 ↗ |
| Action | Restore | “partial to full correction of ADA expression” PMID 19652199 ↗ Aug 2009 |
| Route | Other | “infusions of autologous PBL and/or HSC transduced with retroviral vectors encoding ADA” NCT00599781 ↗ |
| Target | ADA | “retroviral vectors encoding ADA” NCT00599781 ↗ |