Drugs / scAAV9/JeT-GAN
last change Mar 2026 re-read 3 minutes ago

scAAV9/JeT-GAN

Gene therapy (AAV / viral vector)

Developed for
giant axonal neuropathy
Investigated by
University of Texas Southwestern Medical Center

Trials 1

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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1 NCT07543991 Mar 2026 → Dec 2031 expected giant axonal neuropathy University of Texas Southwestern Medical Center Recruiting No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 2 sources stand behind the page.

FieldValueCited text
Known as scAAV9/JeT-GAN ClinicalTrials.gov intervention name — accepted as the source's own label NCT07543991 ↗
Modality Gene therapy (AAV / viral vector) “scAAV9/JeT-GAN (a self-complementary adeno-associated virus-based gene therapy containing the GAN transgene)” PMID 38507752 ↗ Mar 2024
Route Other “a single injection of scAAV9/JeT-GAN, given directly into the left vagus nerve” NCT07543991 ↗