Drugs / Belcesiran
last change May 2024 re-read 3 minutes ago

Belcesiran

also known as DCR-A1AT · DCR-S1459
Developed for
alpha 1-antitrypsin deficiency
Investigated by
Dicerna Pharmaceuticals, Inc.

Trials 3

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT04174118 Oct 2019 → Jul 2021 alpha 1-antitrypsin deficiency Dicerna Pharmaceuticals, Inc. Completed No outcome recorded
Phase 22 trials
Phase 2 NCT05146882 Dec 2021 → May 2022 alpha 1-antitrypsin deficiency Dicerna Pharmaceuticals, Inc. Withdrawn No outcome recorded Stop: Enrollment
Phase 2 NCT04764448 Feb 2021 → Dec 2023 alpha 1-antitrypsin deficiency Dicerna Pharmaceuticals, Inc. Terminated No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 4 sources stand behind the page.

FieldValueCited text
Known as Belcesiran ClinicalTrials.gov intervention name — accepted as the source's own label NCT04764448 ↗
2

NCT04174118 ↗

NCT05146882 ↗

Known as DCR-A1AT “This is a research study to test an experimental study drug (belcesiran, also known as DCR-A1AT).” NCT04174118 ↗
Known as DCR-S1459 ChEMBL registry synonym — accepted as the source's own label CHEMBL4650380 ↗
Route Subcutaneous “belcesiran will be administered subcutaneously (SC) at dose levels planned.” NCT04174118 ↗