Drugs / GenPHSat
last change Jul 2025 re-read 3 minutes ago

GenPHSat

Cell therapy

Developed for
limb-girdle muscular dystrophy
Investigated by
Simone Spuler, MD

Trials 1

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT05588401 Jul 2024 → Jul 2025 limb-girdle muscular dystrophy Simone Spuler, MD Unknown No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as GenPHsat “Participants receive gene edited primary human muscle stem cells (GenPHsat) injection in the left biceps muscle.” NCT05588401 ↗
1

NCT05588401 ↗

Modality Cell therapy “gene edited primary human satellite cell derived muscle stem cells” NCT05588401 ↗
Route Intramuscular “Participants receive gene edited primary human muscle stem cells (GenPHsat) injection in the left biceps muscle.” NCT05588401 ↗