Drugs / AIR001
last change Mar 2026 re-read 3 minutes ago

AIR001

Oligonucleotide (other)

Developed for
pulmonary arterial hypertension · alpha 1-antitrypsin deficiency
Investigated by
Aires Pharmaceuticals, Inc. · AIRNA Corporation

Trials 3

20132014201520162017201820192020202120222023202420252026202720282029
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT07431112 Mar 2026 → Nov 2028 expected alpha 1-antitrypsin deficiency AIRNA Corporation Recruiting No outcome recorded
Phase 22 trials
Phase 2 NCT01725269 Mar 2013 → Apr 2014 pulmonary arterial hypertension Aires Pharmaceuticals, Inc. Terminated No outcome recorded
Phase 2 NCT01725256 Nov 2012 → Feb 2014 pulmonary arterial hypertension Aires Pharmaceuticals, Inc. Terminated No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 3 sources stand behind the page.

FieldValueCited text
Known as AIR001 ClinicalTrials.gov intervention name — accepted as the source's own label NCT01725256 ↗
2

NCT07431112 ↗

NCT01725269 ↗

Modality Oligonucleotide (other) “AIR-001 is an RNA-editing oligonucleotide in sterile preservative-free solution administered by subcutaneous (SC) injection as a single dose.” NCT07431112 ↗
Route Other “inhaled nebulized AIR001 administered” NCT01725256 ↗