Drugs / TS1-ASO
last change Sep 2026 re-read 3 minutes ago

TS1-ASO

Antisense oligonucleotide targets CACNA1C

Developed for
CACNA1C-related disorder
Investigated by
Stanford University

Trials 1

2027202820292030
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT07600658 Sep 2026 → Dec 2029 expected CACNA1C-related disorder Stanford University Not yet recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as TS1-ASO ClinicalTrials.gov intervention name — accepted as the source's own label NCT07600658 ↗
Modality Antisense oligonucleotide “an antisense oligonucleotide (TS1-ASO)” NCT07600658 ↗
Route Intrathecal “Receive intrathecal injections of TS1-ASO via lumbar puncture” NCT07600658 ↗
Target CACNA1C “designed to modulate pre-Messenger RNA (mRNA) splicing of CACNA1C by reducing inclusion of exon 8A and promoting expression of exon 8” NCT07600658 ↗