Drugs / CRISPR_SCD001
last change Aug 2025 re-read 3 minutes ago

CRISPR_SCD001

CRISPR / gene editing

Developed for
sickle cell disease
Investigated by
Mark Walters, MD · University of California, Berkeley · University of California, Los Angeles

Trials 1

20262027202820292030
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT04774536 Aug 2025 → Mar 2030 expected sickle cell disease Mark Walters, MD Recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as CRISPR_SCD001 ClinicalTrials.gov intervention name — accepted as the source's own label NCT04774536 ↗
Action Restore “CRISPRCas9 Corrected Hematopoietic Stem Cells” NCT04774536 ↗
Modality CRISPR / gene editing “cells modified by the CRISPR-Cas9 ribonucleoprotein” NCT04774536 ↗
Route Intravenous “administered by IV infusion” NCT04774536 ↗