Drugs / QRL-201
last change May 2026 re-read 3 minutes ago

QRL-201

Developed for
amyotrophic lateral sclerosis
Investigated by
QurAlis Corporation

Trials 1

2023202420252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1 NCT05633459 Dec 2022 → May 2026 overdue amyotrophic lateral sclerosis QurAlis Corporation Active not recruiting No outcome recorded

News releases announcing trial results or a regulatory action · 6

DateIssuerRelease
2026-02-23 QurAlis Corporation Results QurAlis Demonstrates Effects on Disease Progression and Target Engagement in ANQUR Clinical Trial of QRL-201, a First-in-Class Precision Medicine in Development for Sporadic ALS quralis.com ↗
Results from this study demonstrated QRL-201 had an effect on disease progression in ALS patients; this effect was confirmed by markers of clinical efficacy and changes in a clinically relevant biomarker, along with target engagement.
2024-11-19 QurAlis Corporation Results QurAlis’ ANQUR Clinical Trial of QRL-201 in ALS Advances to Dose Range-Finding (DRF) Phase With First Participant Dosed quralis.com ↗
PK data analysis in dose-escalation phase indicated exposures of QRL-201 met or exceeded the targeted therapeutic range prompting advancement to the DRF phase
2023-07-11 QurAlis Corporation Regulatory QurAlis Receives Clinical Trial Authorisation (CTA) in the U.K. for QRL-201, a First-in-Class STATHMIN-2 Precision Therapy for ALS quralis.com ↗
2023-06-06 QurAlis Corporation Regulatory QurAlis Receives Clinical Trial Authorisation (CTA) in European Union (EU) for QRL-201, a First-in-Class STATHMIN-2 Precision Therapy for ALS quralis.com ↗
2022-12-08 QurAlis Corporation Regulatory QurAlis Receives Health Canada Clinical Trial Application Authorization for QRL-201, a First-in-Class STATHMIN-2 Precision Therapy for ALS quralis.com ↗
2021-12-06 QurAlis Corporation Results QurAlis Presents New Data Confirming Role of STATHMIN-2 in Neuronal Disease Biology at 32nd International Symposium on ALS/MND quralis.com ↗
New research connecting function of STATHMIN-2, TDP-43, and ALS cell biology further validates QRL-201, Company’s lead development candidate in ALS

Evidence & citations 2 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as QRL-201 ClinicalTrials.gov intervention name — accepted as the source's own label NCT05633459 ↗
Route Intrathecal “Multiple ascending doses of QRL-201 will be intrathecally administered to individuals with sporadic ALS.” NCT05633459 ↗