Drugs / SKG0201
last change May 2026 re-read 3 minutes ago

SKG0201

Gene therapy (AAV / viral vector)

Developed for
spinal muscular atrophy, type 1
Investigated by
Kun Sun · Lanyue Biotech (Hangzhou) Co., Ltd.

Trials 2

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/21 trial
Phase 1/2 NCT07554924 May 2026 → May 2029 expected spinal muscular atrophy, type 1 Lanyue Biotech (Hangzhou) Co., Ltd. Not yet recruiting No outcome recorded
Phase not applicable1 trial
— NCT06191354 Jun 2023 → Dec 2025 overdue spinal muscular atrophy, type 1 Kun Sun Active not recruiting No outcome recorded

Evidence & citations 2 cited values

Every value below carries the sentence it was read from. 2 sources stand behind the page.

FieldValueCited text
Known as SKG0201 ClinicalTrials.gov intervention name — accepted as the source's own label NCT07554924 ↗
1

NCT06191354 ↗

Modality Gene therapy (AAV / viral vector) “SKG0201 is a recombinant adeno-associated virus (rAAV) vector-based in vivo gene therapeutic product.” NCT06191354 ↗