Drugs / LV-w1.6 WASp
last change Nov 2019 re-read 3 minutes ago

LV-w1.6 WASp

targets WAS

Developed for
Wiskott-Aldrich syndrome
Investigated by
Genethon · Great Ormond Street Hospital for Children NHS Foundation Trust · Institute of Child Health

Trials 1

20112012201320142015201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT01347242 Mar 2011 → Nov 2019 Wiskott-Aldrich syndrome Genethon Completed No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 2 sources stand behind the page.

FieldValueCited text
Known as LV-w1.6 WASp “treatment of children with a state-of-the-art self-inactivating lentiviral vector (LV-w1.6 WASp) has resulted in significant clinical benefit without inducing selection of...” PMID 28716862 ↗ Jul 2017
Route Other “transplantation of patient's autologous CD34+ cells transduced with lentiviral vector containing human WAS gene” NCT01347242 ↗
Target WAS “lentiviral vector containing the human WAS gene” NCT01347242 ↗