Drugs / nL-ATN1-001
last change Nov 2025 re-read 3 minutes ago

nL-ATN1-001

Antisense oligonucleotide

Developed for
dentatorubral-pallidoluysian atrophy
Investigated by
Dell Children's Medical Center of Central Texas · n-Lorem Foundation

Trials 1

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT07221760 Nov 2025 → Nov 2027 expected dentatorubral-pallidoluysian atrophy n-Lorem Foundation Active not recruiting No outcome recorded

Evidence & citations 2 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as nL-ATN1-001 ClinicalTrials.gov intervention name — accepted as the source's own label NCT07221760 ↗
Modality Antisense oligonucleotide “personalized antisense oligonucleotide (ASO) drug” NCT07221760 ↗