drugset
Drugs / Autologous hematopoietic stem cells genetically modified with GLOBE lentiviral vector encoding for the human beta-globin gene
last change Aug 2019 re-read 3 minutes ago

Autologous hematopoietic stem cells genetically modified with GLOBE lentiviral vector encoding for the human beta-globin gene

targets HBB

Developed for
beta thalassemia
Investigated by
Fondazione Telethon · IRCCS San Raffaele · Orchard Therapeutics

Trials 1

today NCT02453477 · Ph 1/2
201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT02453477 May 2015 → Aug 2019 beta thalassemia IRCCS San Raffaele Unknown No outcome recorded

Evidence & citations 2 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as Autologous hematopoietic stem cells genetically modified with GLOBE lentiviral vector encoding for the human beta-globin gene ClinicalTrials.gov intervention name — accepted as the source's own label NCT02453477 ↗
Target HBB “encoding for the human beta-globin gene” NCT02453477 ↗