Drugs / SAR444836
last change Aug 2023 re-read 3 minutes ago

SAR444836

Gene therapy (AAV / viral vector) targets PAH

Developed for
phenylketonuria
Investigated by
Sanofi

Trials 1

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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT05972629 Aug 2023 → Apr 2030 expected phenylketonuria Sanofi Active not recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as SAR444836 ClinicalTrials.gov intervention name — accepted as the source's own label NCT05972629 ↗
Modality Gene therapy (AAV / viral vector) “an adeno-associated virus (AAV) vector-mediated gene transfer” NCT05972629 ↗
Route Intravenous “Participants will receive a one-time intravenous (IV) administration of SAR444836.” NCT05972629 ↗
Target PAH “gene transfer of human phenylalanine hydroxylase (PAH)” NCT05972629 ↗