Drugs / Trabectedin
last change Aug 2026 re-read 2 minutes ago

Trabectedin

Small molecule targets FLI1 via inhibition

Developed for
leiomyosarcoma · soft tissue sarcoma · sarcoma · liposarcoma · ovarian cancer · myxoid liposarcoma · cancer · bone neoplasm
+43 more · breast cancer · Ewing sarcoma · fallopian tube cancer · metastatic neoplasm · ovarian neoplasm · prostate cancer · round cell liposarcoma · solitary fibrous tumor · synovial sarcoma · cancer of unknown primary site · central nervous system neoplasm · childhood malignant neoplasm · chronic lymphocytic leukemia/small lymphocytic lymphoma · dedifferentiated liposarcoma · desmoplastic small round cell tumor · DNA repair disease · endometrial cancer · endometrium neoplasm · epithelioid sarcoma · gastrointestinal stromal tumor · hemangioendothelioma · hereditary neoplastic syndrome · leiomyosarcoma of the corpus uteri · malignant epithelial tumor of ovary · malignant mesothelioma · malignant pleural mesothelioma · meningioma · mesenchymal chondrosarcoma · metastatic malignant neoplasm · ovarian carcinoma · ovarian carcinosarcoma · ovary leiomyosarcoma · pancreatic adenocarcinoma · peripheral primitive neuroectodermal tumor · peritoneum cancer · pleomorphic liposarcoma · primary peritoneal carcinoma · rhabdomyosarcoma · small intestine cancer · undifferentiated pleomorphic sarcoma · undifferentiated round cell sarcoma · uterine carcinosarcoma · uterine corpus sarcoma
Investigated by
PharmaMar · Johnson & Johnson Pharmaceutical Research & Development, L.L.C. · National Cancer Institute (NCI) · Italian Sarcoma Group · Janssen Research & Development, LLC · Mario Negri Institute for Pharmacological Research
+55 more · Spanish Group for Research in Sarcomas · AstraZeneca · European Organisation for Research and Treatment of Cancer - EORTC · Institut Bergonié · Fondazione Policlinico Universitario Agostino Gemelli IRCCS · Fred Hutchinson Cancer Center · Gustave Roussy, Cancer Campus, Grand Paris · Janssen Scientific Affairs, LLC · Children's Oncology Group · French Sarcoma Group · Gynecologic Oncology Group · Istituto Di Ricerche Farmacologiche Mario Negri · M.D. Anderson Cancer Center · Memorial Sloan Kettering Cancer Center · Sarcoma Alliance for Research through Collaboration · Sarcoma Oncology Research Center, LLC · Anturec Pharmaceuticals GmbH · Averion International Corporation · Bristol-Myers Squibb · Catholic University of the Sacred Heart · Centre Leon Berard · Centre Oscar Lambret · Dana-Farber Cancer Institute · EMD Serono · Fondazione IRCCS Istituto Nazionale dei Tumori, Milano · German Cancer Research Center · Heidelberg University · Hoffmann-La Roche · Humanitas Hospital, Italy · IRCCS San Raffaele · Institut Claudius Regaud · Institut für Klinische Krebsforschung IKF GmbH at Krankenhaus Nordwest · Janssen Pharmaceuticals · Ligue contre le cancer, France · Ludwig-Maximilians - University of Munich · Massachusetts General Hospital · National Center for Tumor Diseases, Heidelberg · National Institutes of Health (NIH) · National Research Agency, France · Northwell Health · Oncopole · Oregon Health and Science University · PharmaMar S.A.U. · Presage Biosciences · Study Group of Bone Tumors · UNICANCER · University Hospital, Marseille · University Medicine Greifswald · University of Colorado, Denver · University of Miami · University of Michigan Rogel Cancer Center · University of Münster · University of Texas Southwestern Medical Center · University of Washington · Xian-Janssen Pharmaceutical Ltd.

Regulatory milestones approvals, filings & regulatory actions · 4 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansion US (FDA) YONDELIS 2018-06-29 fda.gov
Approved US (FDA) YONDELIS 2015-10-23 fda.gov
Approved EU (EMA) Yondelis 2007-09-17 europa.eu
Refused (EMA) EU (EMA) Yondelis 2004-09-07 europa.eu

Trials 78 · started per year

today
EU approved 2007
US approved 2015
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19961997199819992000200120022003200420052006200720082009201020112012201320142015201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 114 trials
Phase 1 NCT03884972 Jun 2019 → Mar 2020 chronic lymphocytic leukemia/small lymphocytic lymphoma M.D. Anderson Cancer Center Withdrawn No outcome recorded
Phase 1 NCT03437070 Jun 2019 → Jun 2021 leiomyosarcoma University of Miami Withdrawn No outcome recorded
Phase 1 NCT03496519 Oct 2018 → Oct 2021 cancer University of Colorado, Denver Withdrawn No outcome recorded
Phase 1 NCT03985722 Sep 2018 → Feb 2021 soft tissue sarcoma Spanish Group for Research in Sarcomas Unknown No outcome recorded
Phase 1 NCT03085225 May 2017 → Nov 2020 ovarian carcinoma, soft tissue sarcoma Institut Bergonié Completed No outcome recorded
Phase 1 NCT03056599 Dec 2016 → Jul 2021 soft tissue sarcoma Presage Biosciences Completed No outcome recorded
Phase 1 NCT02398058 Jul 2014 → Dec 2019 bone neoplasm, soft tissue sarcoma Italian Sarcoma Group Completed No outcome recorded
Phase 1 NCT01426633 Nov 2011 → Dec 2014 leiomyosarcoma, liposarcoma Heidelberg University Completed No outcome recorded
Phase 1 NCT01273480 Dec 2010 → Oct 2012 metastatic neoplasm Janssen Research & Development, LLC Completed No outcome recorded
Phase 1 NCT01273493 Dec 2010 → Apr 2014 liver disorder, metastatic neoplasm Janssen Research & Development, LLC Completed No outcome recorded
Phase 1/25 trials
Phase 1/2 NCT04067115 Jan 2021 → Apr 2025 Ewing sarcoma Sarcoma Alliance for Research through Collaboration Completed No outcome recorded
Phase 1/2 NCT03074318 Sep 2017 → Nov 2020 leiomyosarcoma, liposarcoma Fred Hutchinson Cancer Center Terminated No outcome recorded
Phase 1/2 NCT02805725 Dec 2015 → Apr 2020 soft tissue sarcoma Institut Bergonié Completed No outcome recorded
Phase 1/2 NCT02275286 Nov 2014 → Jun 2028 expected leiomyosarcoma, myxoid liposarcoma, pleomorphic liposarcoma Spanish Group for Research in Sarcomas Recruiting No outcome recorded
Phase 1/2 NCT01267084 Feb 2011 → Nov 2012 metastatic malignant neoplasm Janssen Research & Development, LLC Completed No outcome recorded
Phase 243 trials
Phase 2 NCT07076186 Oct 2025 → Dec 2027 leiomyosarcoma M.D. Anderson Cancer Center Suspended No outcome recorded
Phase 2 NCT06524583 Jan 2025 → Dec 2029 expected leiomyosarcoma UNICANCER Recruiting No outcome recorded
Phase 2 NCT04794127 Feb 2022 → Sep 2024 dedifferentiated liposarcoma, myxoid liposarcoma, round cell liposarcoma Mario Negri Institute for Pharmacological Research Completed No outcome recorded
Phase 2 NCT04383119 Oct 2021 → Dec 2026 expected ovary leiomyosarcoma Italian Sarcoma Group Recruiting No outcome recorded
Phase 2 NCT04305548 Sep 2021 → Dec 2026 expected mesenchymal chondrosarcoma Italian Sarcoma Group Recruiting No outcome recorded
Phase 2 NCT04535271 Sep 2021 → Sep 2028 expected leiomyosarcoma Sarcoma Oncology Research Center, LLC Recruiting No outcome recorded
Phase 2 NCT05131386 May 2021 → Jul 2024 bone neoplasm, undifferentiated round cell sarcoma Spanish Group for Research in Sarcomas Unknown No outcome recorded
Phase 2 NCT04887961 Oct 2020 → Apr 2022 Fondazione Policlinico Universitario Agostino Gemelli IRCCS Unknown No outcome recorded
Phase 2 NCT04076579 Mar 2020 → Jan 2023 sarcoma University of Michigan Rogel Cancer Center Completed No outcome recorded
Phase 2 NCT03886311 May 2019 → Dec 2030 expected sarcoma Sarcoma Oncology Research Center, LLC Recruiting No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT01189253 May 2011 → Jun 2013 sarcoma European Organisation for Research and Treatment of Cancer - EORTC Terminated No outcome recorded
Phase 312 trials
Phase 3 NCT05597917 Oct 2021 → Aug 2026 overdue soft tissue sarcoma University of Münster Recruiting No outcome recorded
Phase 3 NCT03773510 Feb 2019 → Oct 2025 leiomyosarcoma, liposarcoma, synovial sarcoma Italian Sarcoma Group Withdrawn No outcome recorded
Phase 3 NCT02997358 Jan 2017 → Jul 2021 leiomyosarcoma Gustave Roussy, Cancer Campus, Grand Paris Completed No outcome recorded
Phase 3 NCT02903004 Apr 2016 → Dec 2018 ovarian neoplasm Fondazione Policlinico Universitario Agostino Gemelli IRCCS Completed No outcome recorded
Phase 3 NCT02672527 Jan 2015 → Jul 2018 soft tissue sarcoma Gustave Roussy, Cancer Campus, Grand Paris Completed No outcome recorded
Phase 3 NCT01846611 Oct 2013 → Jan 2018 fallopian tube cancer, ovarian cancer, peritoneum cancer Janssen Research & Development, LLC Completed No outcome recorded
Phase 3 NCT01692678 Aug 2012 → Oct 2016 liposarcoma Xian-Janssen Pharmaceutical Ltd. Completed No outcome recorded
Phase 3 NCT01710176 Jun 2011 → Jun 2024 soft tissue sarcoma Italian Sarcoma Group Completed No outcome recorded
Phase 3 NCT01343277 Jun 2011 → Jan 2015 Janssen Research & Development, LLC Completed No outcome recorded
Phase 3 NCT01379989 Jun 2011 → Dec 2020 ovarian cancer Mario Negri Institute for Pharmacological Research Completed No outcome recorded
Phase not applicable1 trial
NCT04008238 Jan 2020 → Aug 2024 desmoplastic small round cell tumor, epithelioid sarcoma, hemangioendothelioma, solitary fibrous tumor +2 Institut Bergonié Completed No outcome recorded
Phase not stated2 trials
NCT01427582 soft tissue sarcoma University of Texas Southwestern Medical Center No longer available No outcome recorded
NCT00210665 sarcoma Janssen Research & Development, LLC No longer available No outcome recorded
Also used as a comparator or background therapy in 8 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT07444619 Background Jun 2026 → Dec 2031 expected soft tissue sarcoma M.D. Anderson Cancer Center Recruiting No outcome recorded
Phase 22 trials
Phase 2 NCT06333314 Comparator Jul 2024 → Oct 2028 expected adrenal cortex carcinoma, carcinoma of the ampulla of vater, duodenal adenocarcinoma, gastric adenocarcinoma +3 UNICANCER Recruiting No outcome recorded
Phase 2 NCT03838744 Comparator May 2020 → Nov 2024 soft tissue sarcoma Italian Sarcoma Group Completed No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT05432791 Comparator Mar 2023 → Aug 2024 overdue leiomyosarcoma of the corpus uteri National Cancer Institute (NCI) Active not recruiting No outcome recorded
Phase 34 trials
Phase 3 NCT06263231 Comparator Jun 2024 → Dec 2027 expected soft tissue sarcoma Intensity Therapeutics, Inc. Active not recruiting No outcome recorded
Phase 3 NCT04979442 Comparator Jul 2021 → Oct 2023 dedifferentiated liposarcoma Rain Oncology Inc Terminated No outcome recorded
Phase 3 NCT03690739 Comparator Aug 2019 → Mar 2021 ovarian carcinoma AGO Research GmbH Terminated No outcome recorded
Phase 3 NCT02929394 Comparator Nov 2017 → Jun 2020 soft tissue sarcoma European Organisation for Research and Treatment of Cancer - EORTC Terminated No outcome recorded

Evidence & citations 10 cited values

Every value below carries the sentence it was read from. 93 sources stand behind the page.

FieldValueCited text
Known as Trabectedin Trabectedin 580 mcg/m2 once weekly for 3 consecutive weeks (Treatment A) or 1,300 mcg/m2 once every 21 days (Treatment B) will be given to patients” NCT00050427
83

Trabectedin (also referred to as Yondelis) is a drug being developed to treat patients with cancer.” NCT00060944

“Doxorubicin and ifosfamide or doxorubicin monotherapy or doxorubicin and trabectedin.” NCT06333314

Trabectedin Presentation: vials with trabectedin 1 mg and sucrose 400 mg.” NCT01104298

“Study drugs include trabectedin and rifampin.” NCT01273480

NCT00003939

NCT01735071

NCT07076186

NCT00379145

NCT04794127

NCT00027508

NCT00210665

NCT03690739

NCT04535271

NCT00050440

NCT03884972

NCT03056599

NCT04887961

NCT01189253

NCT01426633

NCT02903004

NCT02398058

NCT02359474

NCT01427582

NCT05432791

NCT00017030

NCT05131386

NCT04076579

NCT01692678

NCT02805725

NCT00072670

NCT02929394

NCT00580112

NCT03074318

NCT04008238

NCT04067115

NCT03023124

NCT03590210

NCT04305548

NCT01772979

NCT03437070

NCT00569673

NCT03127215

NCT01273493

NCT00050414

NCT03773510

NCT00579501

NCT07444619

NCT06263231

NCT02194231

NCT02234050

NCT01343277

NCT01379989

NCT02672527

NCT01453283

NCT02997358

NCT03838744

NCT02131480

NCT03985722

NCT02247544

NCT00786838

NCT02275286

NCT00070109

NCT02993705

NCT01267084

NCT00002904

NCT02066675

NCT05597917

NCT03496519

NCT01710176

NCT06524583

NCT03397186

NCT03886311

NCT00102609

NCT04383119

NCT02249702

NCT03085225

NCT00796120

NCT01303094

NCT00005625

NCT00113607

NCT01339754

NCT04979442

NCT01846611

Known as Ecteinascidin “A Randomized, Multicenter, Open-label Study of Yondelis (ET-743 Ecteinascidin) Administered by 2 Different Schedules” NCT00060944
Known as Ecteinascidin-743 “While investigating the novel anticancer drug ecteinascidin 743 (Et743), a natural marine product isolated from the Caribbean sea squirt, we discovered a new cell-killing...” PMID 11479630 Aug 2001
2

“Trabectedin (ecteinascidin-743, ET-743, YONDELIS [R])” NCT01453283

NCT00006463

Known as ET-743 “The cytotoxic activity of ecteinascidin 743 (ET-743), a natural product derived from the marine tunicate Ecteinascidia turbinata that exhibits potent anti-tumor activity in...” PMID 11304695 May 2001
6

“While investigating the novel anticancer drug ecteinascidin 743 (Et743), a natural marine product isolated from the Caribbean sea squirt, we discovered a new cell-killing...” PMID 11479630 Aug 2001

“A Randomized, Multicenter, Open-label Study of Yondelis (ET-743 Ecteinascidin) Administered by 2 Different Schedules” NCT00060944

“A phase II study of ET-743/trabectedin ('Yondelis') for patients with advanced gastrointestinal stromal tumours.” PMID 15177491 Jun 2004

ET-743, Yondelis (vials of 1 mg). Route of administration: intravenous infusion” NCT05131386

“Trabectedin (ecteinascidin-743, ET-743, YONDELIS [R])” NCT01453283

NCT00147212

Known as YONDELIS “PURPOSE: To determine the dose-limiting toxicity (DLT) and the maximum tolerated dose of ecteinascidin-743 (ET-743, Yondelis) in children with refractory solid tumors, to...” PMID 15701855 Jan 2005
9

“A Study Comparing the Combination of Trabectedin (YONDELIS) and DOXIL/CAELYX With DOXIL/CAELYX for the Treatment of Advanced-Relapsed Epithelial Ovarian, Primary Peritoneal, or...” NCT01846611

“A Randomized, Multicenter, Phase III Trial of Trabectedin (Yondelis) Versus Doxorubicin-based Chemotherapy as First-Line Therapy in Patients With Translocation-Related Sarcomas (TRS)” NCT00796120

“A Multicenter Phase II Clinical Trial of Neoadjuvant Trabectedin (Yondelis) in Patients With Localized Myxoid / Round Cell Liposarcoma” NCT00579501

“A Randomized Controlled Study of YONDELIS (Trabectedin) or Dacarbazine for the Treatment of Advanced Liposarcoma or Leiomyosarcoma” NCT01343277

“A phase II study of ET-743/trabectedin ('Yondelis') for patients with advanced gastrointestinal stromal tumours.” PMID 15177491 Jun 2004

“The purpose of the study is to determine the dose of the combination of trabectedin (Yondelis) and Doxorubicin” NCT00102609

“combination of trabectedin (Yondelis®)” NCT04887961

“Trabectedin 1 MG [Yondelis]” NCT04067115

NCT00060944

Known as YONDELIS [R] “Trabectedin (ecteinascidin-743, ET-743, YONDELIS [R])” NCT01453283
Action Inhibit “ET-743 downregulated TLS:CHOP expression” PMID 22293175 Feb 2012
Modality Small molecule “Trabectedin (ET-743) is a marine alkaloid isolated from the Caribbean tunicate Ecteinascidia turbinata, with a chemical structure characterized by three fused...” PMID 20647340 Jul 2010
Route Intravenous “administered as a single intravenous infusion” NCT00002904
Target FLI1 “Trabectedin above a threshold concentration reverses the activity of EWS::FLI1 and is potentiated by low-dose irinotecan in vivo.” PMID 41991689 Apr 2026