Drugs / ALXN2350
last change Oct 2025 re-read 3 minutes ago

ALXN2350

Gene therapy (AAV / viral vector)

Developed for
dilated cardiomyopathy 1HH
Investigated by
Alexion Pharmaceuticals, Inc.

Trials 1

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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT07218887 Oct 2025 → Jan 2032 expected dilated cardiomyopathy 1HH Alexion Pharmaceuticals, Inc. Recruiting No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as ALXN2350 ClinicalTrials.gov intervention name — accepted as the source's own label NCT07218887 ↗
Modality Gene therapy (AAV / viral vector) “ALXN2350 is a gene therapy product consisting of an AAV9 capsid containing BAG3 transgene.” NCT07218887 ↗
Route Intravenous “It is administered as a single intravenous (IV) infusion.” NCT07218887 ↗