Drugs / SRP-6004
last change Jun 2025 re-read 3 minutes ago

SRP-6004

Gene therapy (AAV / viral vector) targets DYSF

Developed for
limb-girdle muscular dystrophy
Investigated by
Sarepta Therapeutics, Inc.

Trials 1

202420252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1 NCT05906251 May 2023 → Jun 2025 limb-girdle muscular dystrophy Sarepta Therapeutics, Inc. Terminated No outcome recorded Stop: Business

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as SRP-6004 ClinicalTrials.gov intervention name — accepted as the source's own label NCT05906251 ↗
Modality Gene therapy (AAV / viral vector) “rAAVrh74.MHCK7.DYSF.DV” NCT05906251 ↗
Route Intravenous “Single IV infusion of SRP-6004” NCT05906251 ↗
Target DYSF “rAAVrh74.MHCK7.DYSF.DV” NCT05906251 ↗