Drugs / ST-920
last change Aug 2026 re-read 3 minutes ago

ST-920

Gene therapy (AAV / viral vector)

Developed for
Fabry disease
Investigated by
Sangamo Therapeutics

Trials 1

2020202120222023202420252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT04046224 Jul 2019 → Apr 2025 Fabry disease Sangamo Therapeutics Completed No outcome recorded

Press releases naming this drug 1 release

DateIssuerRelease
2026-08-12 PTC Therapeutics PTC to Expand Rare Disease Portfolio with Acquisition of BLA-Stage ST-920 Fabry Disease Program ptcbio.com ↗

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as ST-920 ClinicalTrials.gov intervention name — accepted as the source's own label NCT04046224 ↗
Action Restore “ST-920 aims to provide stable, long-term production of α-Gal A at therapeutic levels” NCT04046224 ↗
Modality Gene therapy (AAV / viral vector) “an adeno-associated virus (AAV2/6) vector encoding the complementary deoxyribonucleic acid (cDNA) for human a-Gal A” NCT04046224 ↗
Route Intravenous “patients will be infused intravenously with a single dose of ST-920” NCT04046224 ↗