Drugs / scAAV2-P1ND4v2
last change Mar 2025 re-read 3 minutes ago

scAAV2-P1ND4v2

Developed for
Leber hereditary optic neuropathy
Investigated by
Byron Lam · National Eye Institute (NEI)

Trials 1

2015201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1 NCT02161380 Jul 2014 → Mar 2023 Leber hereditary optic neuropathy Byron Lam Completed No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as scAAV2-P1ND4v2 ClinicalTrials.gov intervention name — accepted as the source's own label NCT02161380 ↗
Action Restore “scAAV2-P1ND4v2 (abbreviated as AAV-ND4) gene replacement therapy” NCT02161380 ↗
Route Intravitreal “a single intravitreal injection” NCT02161380 ↗