Drugs / ANB-004
last change Sep 2025 re-read 3 minutes ago

ANB-004

Gene therapy (AAV / viral vector) targets SNRPN

Developed for
spinal muscular atrophy
Investigated by
Biocad

Trials 1

2023202420252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT05747261 Feb 2023 → Sep 2025 overdue spinal muscular atrophy Biocad Recruiting No outcome recorded

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as ANB-004 ClinicalTrials.gov intervention name — accepted as the source's own label NCT05747261 ↗
Modality Gene therapy (AAV / viral vector) “Adeno-associated viral vector carrying the SMN gene” NCT05747261 ↗
Route Intravenous “each of whom will receive a pre-specified cohort dose of ANB-004 as a single intravenous infusion.” NCT05747261 ↗
Target SMN “Adeno-associated viral vector carrying the SMN gene” NCT05747261 ↗