Drugs / HMI-103
last change Sep 2023 re-read 3 minutes ago

HMI-103

Gene therapy (AAV / viral vector)

Developed for
phenylketonuria
Investigated by
Homology Medicines, Inc

Trials 1

2023202420252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1 NCT05222178 Jun 2022 → Sep 2023 phenylketonuria Homology Medicines, Inc Terminated No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as HMI-103 ClinicalTrials.gov intervention name — accepted as the source's own label NCT05222178 ↗
Modality Gene therapy (AAV / viral vector) “HMI-103 is an AAVHSC15 capsid containing a functional copy of the human PAH gene” NCT05222178 ↗
Route Intravenous “HMI-103 Administered Intravenously” NCT05222178 ↗