Drugs / hLB-001
last change Jan 2023 re-read 3 minutes ago

hLB-001

Gene therapy (AAV / viral vector)

Developed for
methylmalonic acidemia
Investigated by
Alexion Pharmaceuticals, Inc. · LogicBio Therapeutics, Inc

Trials 1

20222023202420252026
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT04581785 May 2021 → Jan 2023 methylmalonic acidemia LogicBio Therapeutics, Inc Terminated No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as hLB-001 ClinicalTrials.gov intervention name — accepted as the source's own label NCT04581785 ↗
Modality Gene therapy (AAV / viral vector) “hLB-001 is a liver-targeted, recombinant engineered adeno-associated viral (rAAV) vector” NCT04581785 ↗
Route Intravenous “hLB-001 via IV infusion” NCT04581785 ↗