drugset / Trial / NCT00004293
Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease
Phase 2
Unknown
24 enrolled
National Center for Research Resources (NCRR)
University of Pittsburgh · collab
Treatment
Summary
OBJECTIVES: I. Evaluate the efficacy and toxicity of glucocerebrosidase enzyme therapy in patients with Gaucher disease.
Timeline
- Start
- 1999-11
- Primary completion
- —
- Completion
- —
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Glucocerebrosidase | Protein / enzyme biologic | — | Intravenous |