drugset / Trial / NCT00004498

Phase I Study of Adenoviral Vector Mediated Gene Transfer for Ornithine Transcarbamylase in Adults With Partial Ornithine Transcarbamylase Deficiency

NCT00004498 ↗

Phase 1 Terminated 21 enrolled University of Pennsylvania
Treatment

Summary

OBJECTIVES: I. Determine the safety, feasibility, and potential efficacy of intravascular adenoviral vector mediated gene transfer in the liver in adults with partial ornithine transcarbamylase deficiency.

Timeline

Start
1998-07
Primary completion
—
Completion
2000-09

Drugs

EvaluationDrugModalityDoseRoute
Subject Adenoviral Vector-Mediated Gene Transfer Unknown — Other