drugset / Trial / NCT00004767

Phase II Study of Sodium Phenylbutyrate, Sodium Benzoate, Sodium Phenylacetate, and Dietary Intervention for Urea Cycle Disorders

NCT00004767

Treatment

Summary

OBJECTIVES: I. Assess the safety and efficacy of sodium phenylbutyrate, sodium benzoate, sodium phenylacetate, and dietary intervention in patients with urea cycle disorders.

Timeline

Start
1985-01
Primary completion
Completion

Drugs

EvaluationDrugModalityDoseRoute
Subject Sodium Benzoate Small molecule Intravenous
Subject Sodium Phenylacetate Small molecule Intravenous
Subject Sodium Phenylbutyrate Small molecule Oral