Safety and Efficacy of Recombinant Adeno-Associated Virus Containing the CFTR Gene in the Treatment of Cystic Fibrosis

Phase 2/3 Terminated 100 enrolled Targeted Genetics Corporation Cystic Fibrosis Foundation · collab

RandomizedParallel-groupDouble-blindTreatment

Summary

The purpose of this study is to confirm the improvement in pulmonary function and cytokine levels observed in the recently completed multidose aerosol study for the treatment of Cystic Fibrosis (CF).

Timeline

Start: 2003-06
Primary completion: —
Completion: 2005-10

Drugs

Evaluation	Drug	Modality	Dose	Route
Subject	tgAAVCF	Gene therapy (AAV / viral vector)	—	Inhaled

Safety and Efficacy of Recombinant Adeno-Associated Virus Containing the CFTR Gene in the Treatment of Cystic Fibrosis

Summary

Timeline

Drugs

Indications